Our Pipeline

Using our proprietary drug discovery platform, we are developing a pipeline of first in class precision therapeutics that regulate key muscle proteins to address a broad array of genetically characterized muscle disorders. We have retained global development and commercialization rights to all of our programs. Our current pipeline is summarized below.

PROGRAM

INDICATIONS

Preclinical

Phase 1

Phase 2

Pivotal/
Phase 3

Regulatory Submission

skeletal

EDG-5506

Myosin ATPase

Becker

Preclinical

Phase 1

Phase 2

Pivotal/
Phase 3

Regulatory Submission

EDG-5506

Myosin ATPase

Duchenne

Preclinical

Phase 1

Phase 2

Pivotal/
Phase 3

Regulatory Submission

EDG-5506

Myosin ATPase

LGMD2i, McArdle

Preclinical

Phase 1

Phase 2

Pivotal/
Phase 3

Regulatory Submission

cardiovascular

EDG-7500

Undisclosed Sarcomeric Target

HCM

Preclinical

Phase 1

Phase 2

Pivotal/
Phase 3

Regulatory Submission

EDG-003

Undisclosed Target

Cardiometabolic

Preclinical

Phase 1

Phase 2

Pivotal/
Phase 3

Regulatory Submission

Duchenne - Duchenne muscular dystrophy
Becker - Becker muscular dystrophy
HCM - Hypertrophic cardiomyopathy
LGMD - Limb-girdle muscular dystrophy