Develop new therapies for the treatment of patients with debilitating musculoskeletal disease using uncompromising standards of scientific rigor, personal integrity, and a deep respect for those whose lives we touch.
Understanding how the dystrophin protein complex protects muscle from injury and strategies to mitigate disease when it is missing or defective such as in Duchenne muscular dystrophy.
We’re proud to be working for patients. Learn more about muscular dystrophy, find patient advocacy groups and get the latest information on upcoming clinical trials.
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