Patients & Families
Patients and families are at the core of our mission
As we work towards developing new medicines, we seek to keep the needs, experiences, and hopes of individuals with serious skeletal and cardiac muscle diseases and their families front and center.
For disease-specific resources and support, explore the links below.
How do others face the challenges of serious muscle diseases?
Discover the inspiration, hope and strength that define the lives of people living with serious muscle diseases like Becker and Duchenne.
Romitos: Dominic, Collin & Kaleb
Living with Duchenne.
Brothers. Explorers. Gamers.
Our Guiding Principles
Start with patients. Consider the voice of the patient at every step of the way.
Create and follow the science to lead us to novel therapies.
Work with uncompromising standards and integrity
Communicate honestly, openly and compliantly
Meet the challenge with urgency
Our goal is to understand the challenges individuals living with the diseases we work in, their families and their caregivers face every day to help us develop meaningful treatments. By doing this we can better serve the communities we serve and improve all aspects of our work to develop impactful and potentially life-changing treatments.
Meet Edgewise Patient Advocacy
We help people with serious muscle diseases connect with helpful resources.
Abby Bronson
Head of Patient Advocacy and External Innovation
Katherine Krieger
Director Patient Advocacy
Sarah Tencer
Associate Director, Patient Advocacy
Our goals as patient advocates
- Listen to people living with serious muscle diseases and integrate these learnings into our business approach to all stages of our work developing meaningful and potential life changing treatments
- Connect people living with serious muscle diseases, clinicians, scientists, and regulators to find new and better treatments
- Partner with advocacy organizations to align on community needs and shared goals
- Provide resources to help educate individuals and families
